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Thread: Gene therapy research & treatments

  1. #1
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    waltky's Avatar Senior Member
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    Gene therapy research & treatments

    Drug to fix DNA gets go-ahead...

    Drug to fix faulty DNA gets go-ahead in landmark move that may alter medicine forever
    2 November 2012 | Gene therapy drug given green light for rare disease; Glybera to cost £1m ($1.6m) for each patient; Drug is first to get approval in Western world; EU go-ahead paves way for many more treatments
    Regulators yesterday approved the first therapy in the western world that can correct errors in a person’s genetic code. Europe has approved Glybera to be used against a rare inherited disorder which disrupts fat production in the body. The treatment uses a virus to counteract LPLD, lipoprotein lipase deficiency, which can led to acute inflammation of the pancreas.

    The illness affects around one or two people per million and sufferers have damaged copies of a gene which is essential for breaking down fats. The virus infects muscle cells with a copy of a healthy gene and a one-off treatment is effective. The treatment was backed by an advisory panel to the European Commission in July and full approval was granted yesterday. The medicine should be available next year.

    Professor John Kastelein, of the University of Amsterdam, said the therapy would have a ‘dramatic impact’ on patients. Only two other gene therapies have previously been approved for sale, both in China. It will cost around £1 million ($1.6 million) per patient, a new record for pricey modern medicines.

    Joern Aldag, chief executive of Amsterdam-based uniQure, said more such treatments would follow and argued a high price was justified because gene therapy restored natural body function and was not just a short-term fix. 'This provides higher benefit to patients than the classical protein replacement strategy and this is why we think we should be fairly and adequately compensated,' he said in a telephone interview on Friday

    Read more: http://www.dailymail.co.uk/news/arti...#ixzz2BMLPkXIl

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    Conley (11-05-2012)

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    Calypso Jones's Avatar Senior Member
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    I am assuming you have a particular agenda in posting this, Walt? Is this therapy derived from embryonic stem cells. I rather doubt it.

    Perhaps you assume that conservatives and christians have a problem with adult stem cell research? They don't. It's the growing of the unborn for harvesting their stem cells which in every case have been proven to be not just unsuccessful but catastrophic. Terrifyingly so. They don't call 'em terratomas for nuthin.

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    roadmaster's Avatar Senior Member
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    Perhaps you assume that conservatives and christians have a problem with adult stem cell research? They don't.
    No we don't in fact it's better than the other.

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    Calypso Jones (11-05-2012)

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    Calypso Jones's Avatar Senior Member
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    exactly Roadmaster. Do you have any idea as to Walt's intent. Is he just delighted that 1 or 2 people out of 1million of the population of the world? US? now have mAYBE the potential to MAYBE have their genes manipulated. maybe.

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    Quote Originally Posted by Calypso Jones View Post
    I am assuming you have a particular agenda in posting this, Walt? Is this therapy derived from embryonic stem cells. I rather doubt it.

    Perhaps you assume that conservatives and christians have a problem with adult stem cell research? They don't. It's the growing of the unborn for harvesting their stem cells which in every case have been proven to be not just unsuccessful but catastrophic. Terrifyingly so. They don't call 'em terratomas for nuthin.
    Why are you making all these assumptions?

    It's a very interesting article and the potential to repair genes is huge...this is just the first example on a rare disease, if it works it could theoretically be applied to many more

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    waltky's Avatar Senior Member
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    Cool

    Calypso...

    ... no agenda...

    ... most of my posts are of an informational nature such as this one...

    ... a thread about gene therapy in a health & medicine forum...

    ... also started threads for stem cell posts and a thread for heart related posts...

    ... health & medicine forum...

    ... get it?
    Last edited by waltky; 11-05-2012 at 04:45 PM.

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    Captain Obvious (11-05-2012)

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    Quote Originally Posted by waltky View Post
    Calypso...

    ... no agenda...

    ... most of my posts are of an informational nature such as this one...

    ... a thread about gene therapy in a health & medicine forum...

    ... also started threads for stem cell posts and a thread for heart related posts...

    ... health & medicine forum...

    ... get it?
    You tell 'em, Walt - don't take no $#@!.
    my junk is ugly

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